{"id":6427,"date":"2026-07-08T12:02:31","date_gmt":"2026-07-08T10:02:31","guid":{"rendered":"https:\/\/rijetke-bolesti.com\/?p=6427"},"modified":"2026-07-08T12:04:07","modified_gmt":"2026-07-08T10:04:07","slug":"novo-europsko-odobrenje-prosiruje-mogucnosti-lijecenja-spinalne-misicne-atrofije","status":"publish","type":"post","link":"https:\/\/rijetke-bolesti.com\/en\/novo-europsko-odobrenje-prosiruje-mogucnosti-lijecenja-spinalne-misicne-atrofije\/","title":{"rendered":"Novo europsko odobrenje pro\u0161iruje mogu\u0107nosti lije\u010denja spinalne mi\u0161i\u0107ne atrofije"},"content":{"rendered":"
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Europska komisija odobrila je novu gensku terapiju za lije\u010denje djece starije od dvije godine, adolescenata i odraslih osoba koje \u017eive s 5q spinalnom mi\u0161i\u0107nom atrofijom (SMA). Rije\u010d je o prvom jednokratnom genskom terapijskom pristupu u Europskoj uniji odobrenom za ovu skupinu pacijenata, \u010dime se zna\u010dajno pro\u0161iruju mogu\u0107nosti lije\u010denja. Do sada je ovakav oblik terapije bio dostupan samo djeci do dvije godine \u017eivota.Nakon europskog regulatornog odobrenja slijede nacionalni postupci procjene i dono\u0161enja odluka o dostupnosti terapije u pojedinim dr\u017eavama \u010dlanicama. Hrvatski savez za rijetke bolesti o\u010dekuje da se postupci provedu u razumnim rokovima kako bi terapija bila dostupna pacijentima koji ispunjavaju medicinske kriterije.<\/p>\n\n\n\n


Spinalna mi\u0161i\u0107na atrofija progresivna je rijetka neuromi\u0161i\u0107na bolest koja uzrokuje gubitak mi\u0161i\u0107ne snage i motori\u010dkih funkcija. U Hrvatskoj je potvr\u0111eno 125 osoba koje \u017eive sa SMA, a od 2023. godine bolest se otkriva i kroz novoro\u0111ena\u010dki probir, \u0161to omogu\u0107uje pravodobno lije\u010denje.<\/p>","protected":false},"excerpt":{"rendered":"

Europska komisija odobrila je novu gensku terapiju za lije\u010denje djece starije od dvije godine, adolescenata i odraslih osoba koje \u017eive s 5q spinalnom mi\u0161i\u0107nom atrofijom (SMA). Rije\u010d je o prvom jednokratnom genskom terapijskom pristupu u Europskoj uniji odobrenom za ovu skupinu pacijenata, \u010dime se zna\u010dajno…<\/p>","protected":false},"author":3,"featured_media":0,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"content-type":"","footnotes":""},"categories":[34],"tags":[],"class_list":["post-6427","post","type-post","status-publish","format-standard","hentry","category-rijetka-infoteka"],"yoast_head":"\nNovo europsko odobrenje pro\u0161iruje mogu\u0107nosti lije\u010denja spinalne mi\u0161i\u0107ne atrofije - Hrvatski savez za rijetke bolesti<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/rijetke-bolesti.com\/en\/novo-europsko-odobrenje-prosiruje-mogucnosti-lijecenja-spinalne-misicne-atrofije\/\" \/>\n<meta property=\"og:locale\" content=\"en_GB\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Novo europsko odobrenje pro\u0161iruje mogu\u0107nosti lije\u010denja spinalne mi\u0161i\u0107ne atrofije - Hrvatski savez za rijetke bolesti\" \/>\n<meta property=\"og:description\" content=\"Europska komisija odobrila je novu gensku terapiju za lije\u010denje djece starije od dvije godine, adolescenata i odraslih osoba koje \u017eive s 5q spinalnom mi\u0161i\u0107nom atrofijom (SMA). Rije\u010d je o prvom jednokratnom genskom terapijskom pristupu u Europskoj uniji odobrenom za ovu skupinu pacijenata, \u010dime se zna\u010dajno...\" \/>\n<meta property=\"og:url\" content=\"https:\/\/rijetke-bolesti.com\/en\/novo-europsko-odobrenje-prosiruje-mogucnosti-lijecenja-spinalne-misicne-atrofije\/\" \/>\n<meta property=\"og:site_name\" content=\"Hrvatski savez za rijetke bolesti\" \/>\n<meta property=\"article:published_time\" content=\"2026-07-08T10:02:31+00:00\" \/>\n<meta property=\"article:modified_time\" content=\"2026-07-08T10:04:07+00:00\" \/>\n<meta property=\"og:image\" content=\"https:\/\/rijetke-bolesti.com\/wp-content\/uploads\/2026\/07\/Gemini_Generated_Image_6to3dx6to3dx6to3.png\" \/>\n\t<meta property=\"og:image:width\" content=\"1408\" \/>\n\t<meta property=\"og:image:height\" content=\"768\" \/>\n\t<meta property=\"og:image:type\" content=\"image\/png\" \/>\n<meta name=\"author\" content=\"sara\" \/>\n<meta name=\"twitter:card\" content=\"summary_large_image\" \/>\n<meta name=\"twitter:label1\" content=\"Written by\" \/>\n\t<meta name=\"twitter:data1\" content=\"sara\" \/>\n\t<meta name=\"twitter:label2\" content=\"Estimated reading time\" \/>\n\t<meta name=\"twitter:data2\" content=\"1 minute\" \/>\n<script type=\"application\/ld+json\" class=\"yoast-schema-graph\">{\"@context\":\"https:\/\/schema.org\",\"@graph\":[{\"@type\":\"WebPage\",\"@id\":\"https:\/\/rijetke-bolesti.com\/novo-europsko-odobrenje-prosiruje-mogucnosti-lijecenja-spinalne-misicne-atrofije\/\",\"url\":\"https:\/\/rijetke-bolesti.com\/novo-europsko-odobrenje-prosiruje-mogucnosti-lijecenja-spinalne-misicne-atrofije\/\",\"name\":\"Novo europsko odobrenje pro\u0161iruje mogu\u0107nosti lije\u010denja spinalne mi\u0161i\u0107ne atrofije - 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